Cell stemness Epigenetic changes Fetal growth restriction Gene transfer Mouse model Glucocorticosteroid LMNA Mecp2 AICD CNS Maladie neuromusculaire MRI Microglia ERK1/2 signaling Intra-CSF delivery Cofilin-1 DTI Antisense oligonucleotides Calcium handling Brain damage Biological marker Duchenne Muscular Dystrophy Albumin gene targeting Distal myopathy Clinical markers Amyotrophie spinale Biomarker Prematurity MUNIX Modèle murin Amyotrophic Lateral Sclerosis Intra-uterine growth restriction Brain Cartilage and bone regeneration IRM Brain MRI CRISPR/SaCas9 FGR Blood brain barrier Aav10 Disease heterogeneity SMN Melatonin ALS ASOs Dicer Longitudinal progression Inflammation Diseases Lentiviral vectors Adult patients Disease modifiers Chondrocytes MiRNA Bone involvement DPRs 3xTgAD Mice Effector T cells Functional outcomes Clinical trial Coagulation factor IX Errance diagnotique C9orf72 GABA Neuromuscular disease IPSCs Bioinformatics Genetics Early-onset sepsis Adult SMA Fabry disease lysosomal storage disorders adeno asociated virus-9 Brain imaging Brain injury Biomarkers Bone development MND Icv Clinical trials Les paramètres respiratoires G-Secretase Extremely preterm infants AAV FTD Spinal muscular atrophy IUGR Dilated cardiomyopathy Genetical therapy FOXO3a GeneRide Adenosine Skeletal muscle Cell reprogramming Maternal malnutrition MRNP assembly Maternal behavior Long-term handicap Cellules souches musculaires ASO Gene therapy Brain development